In recent years, the scientific community has made significant strides in the field of gene editing, particularly through the ...
Niemann-Pick disease type C (NPC) is a rare genetic disorder that affects the nervous system and other organs, causing ...
Children with Down’s syndrome have a 150-fold increased risk of developing leukaemia than those without the condition. Now, ...
Miplyffa treats Niemann-Pick disease type C, which progressively impacts the abilities to speak, swallow, and walk or move ...
A rare cause of hereditary cognitive decline known as CSF1R-Related Disorder (CSF1R-RD) gets its name from mutations in the ...
Children's Hospital of Michigan is treating the first person in Michigan with a newly approved gene therapy for beta ...
Scientists have conducted the largest and most diverse study to date on how recessive genetic changes contribute to developmental disorders. They found that most undiagnosed cases that are due to ...
A Detroit Medical Center hospital has begun treating patients with the first gene therapy for beta-thalassemia, a rare blood ...
A common diabetes medication, metformin, slows the growth of precancerous cells in the esophagus while some metabolic ...
BOSTON, Sept. 04, 2024 (GLOBE NEWSWIRE) -- Sensei Biotherapeutics, Inc. (Nasdaq: SNSE), a clinical stage immuno-oncology company focused on the discovery and development of next-generation ...
With the development of advanced genome editing techniques, it is now possible to insert large DNA sequences into precise genomic locations without the need for DNA double strand breaks, enabling the ...